Evaluation of Pharmacokinetic Profile of Novel Ophthalmic Formulation of Loteprednol Etabonate

Friday, April 25, 2014
KIOSKS (Boston Convention and Exhibition Center)
Kim Brazzell, PhD, Kala Pharmaceuticals, Waltham, MA, USA
Lisa R. Schopf, PhD, Kala Pharmaceuticals, Waltham, MA, USA
Elizabeth Enlow, PhD, Kala Pharmaceuticals, Waltham, MA, USA
Alexey Popov, PhD, Kala Pharmaceuticals, Inc., Waltham, MA, USA
James Bourassa, PhD, Kala Pharmaceuticals, Waltham, MA, USA
Hongming Chen, ScD Waltham, MA, USA

Narrative Responses:

Purpose
The purpose of these studies was to evaluate the ocular pharmacokinetic (PK) profile of a novel formulation of loteprednol etabonate that uses a proprietary mucus penetrating particle (MPP) technology. The PK profile of loteprednol etabonate was evaluated after a QD, BID and QID dosing regimen.

Methods
A rabbit model was used for these PK studies. A single drop (QD) of either loteprednol etabonate ophthalmic suspension MPP (LE-MPP) 0.4% or LOTEMAX®-brand loteprednol etabonate ophthalmic gel 0.5% (LE gel) was administered to one group of rabbits.  A second group of rabbits received LE-MPP 0.4% either BID or QID.  Samples of the aqueous humor and cornea were collected over a 12 hour period after a single administration of the test article for QD animal groups, and 8 hours after the last administration for BID/QID animal groups.  Loteprednol etabonate concentrations were assayed by liquid chromatography–tandem mass spectrometry (LC/MS/MS).

Results
Seventy-eight rabbits (156 eyes) were used for the PK analysis.  After a single drop, peak concentrations of loteprednol etabonate in the cornea and aqueous humor were 2580 ng/g and 30.3 ng/mL for LE-MPP 0.4%, and 1470 ng/g and 12.7 ng/mL for the LE gel. Following instillation of multiple drops (BID or QID dosing regimen), peak levels of loteprednol etabonate in the cornea and aqueous humor were 1392 ng/g and 28.3 ng/mL for BID, and 1672 ng/g and 30.3 ng/mL for QID administration of LE-MPP 0.4%.

Conclusion
In these rabbit studies, high levels of loteprednol etabonate were achieved in the cornea and aqueous humor following topical administration of a novel MPP ophthalmic formulation.  These preclinical data indicate penetration of ocular mucosal barriers may present an opportunity to enhance effective drug levels in ocular tissue through topical administration.